Gene editing stories

Jul 21, 2026

Broad Institute, Boston Children's Hospital, and Jackson Laboratory Launch $160 Million Center for Rare Disease Gene Therapies

Three major research institutions announced the creation of the Center for Therapeutic Genetics, a nonprofit collaboration aimed at developing standardized genetic medicines, including base and prime editing, for rare and ultra-rare diseases that currently lack treatments.

Jul 21, 20269 sources

Jul 9, 2026

ARPA-H Launches $160 Million Gene Editing Drug Development Program

The Advanced Research Projects Agency for Health (ARPA-H) has launched a $160 million initiative to fund seven groups over five years to develop custom gene editing drugs, aiming to replicate successes like the Baby KJ case.

Jul 9, 20261 source

Apr 19, 2026

Breakthrough Prize Awards $3 Million to Researchers Behind First Sickle Cell CRISPR Therapy

Dr. Swee Lay Thein and Dr. Stuart Orkin received the $3 million Breakthrough Prize in Life Sciences for research that led to the development of the first CRISPR-based therapy for sickle cell disease.

Apr 19, 20261 source

Top claims

▪The Food and Drug Administration issued draft guidance on June 2, 2026, aimed at streamlining gene therapy development for rare diseases.
▪The Center for Therapeutic Genetics aims to work with regulators to establish standards that allow individualized genetic treatments to function as repeatable clinical procedures rather than unique drugs.
▪The Center for Therapeutic Genetics plans to openly share its design tools, disease models, safety data, manufacturing processes, and clinical protocols to enable other institutions to replicate its treatments.

Subtopics

Drug Approval and Clinical Trials3 Drug development1 Gene therapy1 Precision medicine1 Rare diseases1

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